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Cost-effectiveness of voretigene neparvovec in the treatment of patients with inherited retinal disease with RPE65 mutation in Switzerland

OBJECTIVE: We aimed to evaluate the cost-effectiveness of voretigene neparvovec (VN) compared with standard of care (SoC) for patients with inherited retinal disease (IRD) caused by a biallelic RPE65-mutation. VN is a live, non-replicating adeno-associated virus serotype 2 (AAV2). SoC is best suppor...

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Detalles Bibliográficos
Autores principales:	Bhadhuri, Arjun, Dröschel, Daniel, Guldimann, Mike, Jetschgo, Claudia, Banhazi, Judit, Schwenkglenks, Matthias, Sutherland, C. Simone
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2022
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9241179/ https://www.ncbi.nlm.nih.gov/pubmed/35765055 http://dx.doi.org/10.1186/s12913-022-08211-y

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