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Accelerate Clinical Trials in Charcot-Marie-Tooth Disease (ACT-CMT): A Protocol to Address Clinical Trial Readiness in CMT1A

With therapeutic trials on the horizon for Charcot-Marie-Tooth type 1A (CMT1A), reliable, valid, and responsive clinical outcome assessments and biomarkers are essential. Accelerate Clinical Trials in CMT (ACT-CMT) is an international study designed to address important gaps in CMT1A clinical trial...

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Detalles Bibliográficos
Autores principales:	Eichinger, Katy, Sowden, Janet E., Burns, Joshua, McDermott, Michael P., Krischer, Jeffrey, Thornton, John, Pareyson, Davide, Scherer, Steven S., Shy, Michael E., Reilly, Mary M., Herrmann, David N.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Frontiers Media S.A. 2022
Materias:	Neurology
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9271780/ https://www.ncbi.nlm.nih.gov/pubmed/35832173 http://dx.doi.org/10.3389/fneur.2022.930435

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