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Patient preferences and priorities for haemophilia gene therapy in the US: A discrete choice experiment

INTRODUCTION: Gene therapy has shown promise in clinical trials for patients with haemophilia, but patient preference studies have focused on factor replacement treatments. AIM: We conducted a discrete choice experiment (DCE) to investigate the relative importance and differential preferences patien...

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Detalles Bibliográficos
Autores principales:	Witkop, Michelle, Morgan, George, O'Hara, Jamie, Recht, Michael, Buckner, Tyler W., Nugent, Diane, Curtis, Randall, O'Mahony, Brian, Skinner, Mark W., Mulhern, Brendan, Cawson, Matthew, Ali, Talaha M., Sawyer, Eileen K., Li, Nanxin
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	John Wiley and Sons Inc. 2021
Materias:	Original Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9290457/ https://www.ncbi.nlm.nih.gov/pubmed/34310811 http://dx.doi.org/10.1111/hae.14383

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