Cargando…
Evaluating longitudinal therapy effects via the North Star Ambulatory Assessment
INTRODUCTION/AIMS: In comparative studies, treatment effects are typically evaluated at a specific time point. When data are collected periodically, an alternative, clinically meaningful approach could be used to assess the totality of treatment effects. We applied a well‐developed analytical proced...
Autores principales: | McDonald, Craig M., Wei, Lee‐Jen, Flanigan, Kevin M., Elfring, Gary, Trifillis, Panayiota, Muntoni, Francesco |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
John Wiley & Sons, Inc.
2021
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9290940/ https://www.ncbi.nlm.nih.gov/pubmed/34383312 http://dx.doi.org/10.1002/mus.27396 |
Ejemplares similares
-
Longitudinal Evaluation of Working Memory in Duchenne Muscular Dystrophy
por: Thangarajh, Mathula, et al.
Publicado: (2020) -
Deflazacort versus prednisone/prednisolone for maintaining motor function and delaying loss of ambulation: A post HOC analysis from the ACT DMD trial
por: Shieh, Perry B., et al.
Publicado: (2018) -
The NorthStar Ambulatory Assessment in Duchenne muscular dystrophy: considerations for the design of clinical trials
por: Ricotti, Valeria, et al.
Publicado: (2016) -
Novel approaches to analysis of the North Star Ambulatory Assessment (NSAA) in Duchenne muscular dystrophy (DMD): Observations from a phase 2 trial
por: Muntoni, Francesco, et al.
Publicado: (2022) -
Revised North Star Ambulatory Assessment for Young Boys with Duchenne Muscular Dystrophy
por: Mercuri, Eugenio, et al.
Publicado: (2016)