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Improved attention linked to sustained phenylalanine reduction in adults with early‐treated phenylketonuria

Pegvaliase is approved to reduce phenylalanine (Phe) levels for people with phenylketonuria (PKU). PRISM‐1 (NCT01819727) and PRISM‐2 (NCT01889862) data were analyzed to evaluate the relationship between Phe and inattention in adult participants with PKU. In the modified‐intent‐to‐treat population (N...

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Detalles Bibliográficos
Autores principales:	Bilder, Deborah A., Arnold, Georgianne L., Dimmock, David, Grant, Mitzie L., Janzen, Darren, Longo, Nicola, Nguyen‐Driver, Mina, Jurecki, Elaina, Merilainen, Markus, Amato, Gianni, Waisbren, Susan
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	John Wiley & Sons, Inc. 2021
Materias:	Original Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9299696/ https://www.ncbi.nlm.nih.gov/pubmed/34826353 http://dx.doi.org/10.1002/ajmg.a.62574

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