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Can symptomatic nmDuchenne carriers benefit from treatment with ataluren? Results of 193-month follow-up
Autores principales: | Dori, Amir, Guglieri, Michela, Scutifero, Marianna, Passamano, Luigia, Trabacca, Antonio, Politano, Luisa |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Pacini Editore Srl
2022
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9299955/ https://www.ncbi.nlm.nih.gov/pubmed/35919205 |
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