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Characterization of patients with Becker muscular dystrophy by histology, magnetic resonance imaging, function, and strength assessments
INTRODUCTION/AIMS: Becker muscular dystrophy (BMD) is characterized by variable disease severity and progression, prompting the identification of biomarkers for clinical trials. We used data from an ongoing phase II study to provide a comprehensive characterization of a cohort of patients with BMD,...
Autores principales: | Comi, Giacomo P., Niks, Erik H., Cinnante, Claudia M., Kan, Hermien E., Vandenborne, Krista, Willcocks, Rebecca J., Velardo, Daniele, Ripolone, Michela, van Benthem, Jules J., van de Velde, Nienke M., Nava, Simone, Ambrosoli, Laura, Cazzaniga, Sara, Bettica, Paolo U. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
John Wiley & Sons, Inc.
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9302983/ https://www.ncbi.nlm.nih.gov/pubmed/34918368 http://dx.doi.org/10.1002/mus.27475 |
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