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Gene therapy in haemophilia: literature review and regional perspectives for Turkey

Haemophilia is an X-linked lifelong congenital bleeding disorder that is caused by insufficient levels of factor VIII (FVIII; haemophilia A) or factor IX (FIX; haemophilia B) and characterized by spontaneous and trauma-related bleeding episodes. The cornerstone of the treatment, factor replacement,...

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Detalles Bibliográficos
Autores principales:	Kavaklı, Kaan, Antmen, Bülent, Okan, Vahap, Şahin, Fahri, Aytaç, Selin, Balkan, Can, Berber, Ergül, Kaya, Zühre, Küpesiz, Alphan, Zülfikar, Bülent
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	SAGE Publications 2022
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9310332/ https://www.ncbi.nlm.nih.gov/pubmed/35898436 http://dx.doi.org/10.1177/20406207221104591

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