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Towards gene therapy for IPEX syndrome

Immune dysregulation polyendocrinopathy enteropathy X linked (IPEX) syndrome is an uncurable disease of the immune system, with immune dysregulation that is caused by mutations in FOXP3. Current treatment options, such as pharmacological immune suppression and allogeneic hematopoietic stem cell tran...

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Detalles Bibliográficos
Autores principales:	Borna, Simon, Lee, Esmond, Sato, Yohei, Bacchetta, Rosa
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	John Wiley and Sons Inc. 2022
Materias:	Highlights
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9322407/ https://www.ncbi.nlm.nih.gov/pubmed/35355253 http://dx.doi.org/10.1002/eji.202149210

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