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Clinical and humanistic burden among pediatric patients with neurofibromatosis type 1 and plexiform neurofibroma in the USA

PURPOSE: To assess clinical and humanistic burden among pediatric patients with neurofibromatosis type 1 (NF1) and plexiform neurofibroma (PN) in the USA. METHODS: NF1-PN patients aged 8–18 years (treatment-naïve or ≤ 1 month of selumetinib treatment) and their caregivers and caregivers of similar p...

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Detalles Bibliográficos
Autores principales:	Yang, Xiaoqin, Yoo, Hyun Kyoo, Amin, Suvina, Cheng, Wendy Y., Sundaresan, Sanjana, Zhang, Lujia, Duh, Mei Sheng
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer Berlin Heidelberg 2022
Materias:	Original Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9325812/ https://www.ncbi.nlm.nih.gov/pubmed/35579709 http://dx.doi.org/10.1007/s00381-022-05513-8

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