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Gene Editing to Tackle Facioscapulohumeral Muscular Dystrophy
Facioscapulohumeral dystrophy (FSHD) is a skeletal muscle disease caused by the aberrant expression of the DUX4 gene in the muscle tissue. To date, different therapeutic approaches have been proposed, targeting DUX4 at the DNA, RNA or protein levels. The recent development of the clustered regularly...
Autores principales: | Mariot, Virginie, Dumonceaux, Julie |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2022
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9334676/ https://www.ncbi.nlm.nih.gov/pubmed/35910413 http://dx.doi.org/10.3389/fgeed.2022.937879 |
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