The efficacy and safety of allogeneic stem cell transplantation in Mevalonate Kinase Deficiency

OBJECTIVES: Mevalonate kinase deficiency (MKD) is a rare autoinflammatory syndrome. Several reports have described allogeneic hematopoietic stem cell transplantation in severely affected patients, sometimes with promising results. In view of the scarcity of data, this study aims to analyse the effic...

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Detalles Bibliográficos
Autores principales: Jeyaratnam, Jerold, Faraci, Maura, Gennery, Andrew R., Drabko, Katarzyna, Algeri, Mattia, Morimoto, Akira, Sirait, Tiarlan, Lankester, Arjan C., Albert, Michael, Neven, Benedicte, Frenkel, Joost
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BioMed Central 2022
Materias:
Research Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9338460/
https://www.ncbi.nlm.nih.gov/pubmed/35906690
http://dx.doi.org/10.1186/s12969-022-00716-4

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9338460/
https://www.ncbi.nlm.nih.gov/pubmed/35906690
http://dx.doi.org/10.1186/s12969-022-00716-4

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