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Criteria to define rare diseases and orphan drugs: a systematic review protocol

INTRODUCTION: Rare diseases (RDs) are often chronic and progressive life-threatening medical conditions that affect a low percentage of the population compared with other diseases. These conditions can be treated with medications known as orphan drugs (ODs). Unfortunately, there is no universal defi...

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Detalles Bibliográficos
Autores principales:	Abozaid, Ghada Mohammed, Kerr, Katie, McKnight, Amy, Al-Omar, Hussain A
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BMJ Publishing Group 2022
Materias:	Public Health
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9345065/ https://www.ncbi.nlm.nih.gov/pubmed/35906057 http://dx.doi.org/10.1136/bmjopen-2022-062126

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