Long-Term Biodistribution and Safety of Human Dystrophin Expressing Chimeric Cell Therapy After Systemic-Intraosseous Administration to Duchenne Muscular Dystrophy Model

Duchenne muscular dystrophy (DMD) is a lethal disease caused by X-linked mutations in the dystrophin gene. Dystrophin deficiency results in progressive degeneration of cardiac, respiratory and skeletal muscles leading to premature death due to cardiopulmonary complications. Currently, no cure exists...

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Detalles Bibliográficos
Autores principales: Siemionow, Maria, Brodowska, Sonia, Langa, Paulina, Zalants, Kristina, Kozlowska, Katarzyna, Grau-Kazmierczak, Wictoria, Heydemann, Ahlke
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer International Publishing 2022
Materias:
Original Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9385806/
https://www.ncbi.nlm.nih.gov/pubmed/35978142
http://dx.doi.org/10.1007/s00005-022-00656-7

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