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The Black Box of Technological Outcome Measures: An Example in Duchenne Muscular Dystrophy

BACKGROUND: Outcome measures for non-ambulant Duchenne muscular dystrophy (DMD) patients are limited, with only the Performance of the Upper Limb (PUL) approved as endpoint for clinical trials. OBJECTIVE: We assessed four outcome measures based on devices developed for the gaming industry, aiming to...

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Detalles Bibliográficos
Autores principales:	Naarding, Karin J., Janssen, Mariska M.H.P., Boon, Ruben D., Bank, Paulina J.M., Matthew, Robert P., Kurillo, Gregorij, Han, Jay J., Verschuuren, Jan J.G.M., de Groot, Imelda J.M., van der Holst, Menno, Kan, Hermien E., Niks, Erik H.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	IOS Press 2022
Materias:	Research Report
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9398077/ https://www.ncbi.nlm.nih.gov/pubmed/35723109 http://dx.doi.org/10.3233/JND-210767

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