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Therapeutic Strategies in Huntington’s Disease: From Genetic Defect to Gene Therapy
Despite the identification of an expanded CAG repeat on exon 1 of the huntingtin gene located on chromosome 1 as the genetic defect causing Huntington’s disease almost 30 years ago, currently approved therapies provide only limited symptomatic relief and do not influence the age of onset or disease...
| Autores principales: | , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
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MDPI
2022
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| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9405755/ https://www.ncbi.nlm.nih.gov/pubmed/36009443 http://dx.doi.org/10.3390/biomedicines10081895 |