Changes in Ventilatory Support Requirements of Spinal Muscular Atrophy (SMA) Patients Post Gene-Based Therapies

Spinal muscular atrophy (SMA) is a genetic neuromuscular disease resulting in global muscular weakness and, frequently, in respiratory failure and premature death. Gene-based therapies like Nusinersen are now available for patients with SMA. The aim of this review was to assess in “real world” studi...

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Detalles Bibliográficos
Autores principales: Panagiotou, Panagiota, Kanaka-Gantenbein, Christina, Kaditis, Athanasios G.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2022
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9406975/
https://www.ncbi.nlm.nih.gov/pubmed/36010097
http://dx.doi.org/10.3390/children9081207

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9406975/
https://www.ncbi.nlm.nih.gov/pubmed/36010097
http://dx.doi.org/10.3390/children9081207

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