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PB2314: OLIPUDASE ALFA FOR ADULTS WITH ACID SPHINGOMYELINASE DEFICIENCY: IMPROVEMENTS IN CROSSOVER PLACEBO PATIENTS AND FURTHER IMPROVEMENTS IN ORIGINAL OLIPUDASE ALFA PATIENTS AFTER 2 YEARS IN ASCEND TRIAL
| Autores principales: | , , , , , , , , , , , , , , , , , , , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
Lippincott Williams & Wilkins
2022
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| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9431580/ http://dx.doi.org/10.1097/01.HS9.0000852080.43506.a5 |
| _version_ | 1784780093971759104 |
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| author | Villarrubia, J. Wasserstein, M. Barbato, A. Gallagher, R. C. Giugliani, R. Guelbert, N. B. Hennermann, J. B. Hollak, C. Ikezoe, T. Lachmann, R. Lidove, O. Mabe, P. Mengel, E. Scarpa, M. Senates, E. Tchan, M. Thurberg, B. L. Yarramaneni, A. Rawlings, A. M. Kim, Y. Kumar, M. |
| author_facet | Villarrubia, J. Wasserstein, M. Barbato, A. Gallagher, R. C. Giugliani, R. Guelbert, N. B. Hennermann, J. B. Hollak, C. Ikezoe, T. Lachmann, R. Lidove, O. Mabe, P. Mengel, E. Scarpa, M. Senates, E. Tchan, M. Thurberg, B. L. Yarramaneni, A. Rawlings, A. M. Kim, Y. Kumar, M. |
| author_sort | Villarrubia, J. |
| collection | PubMed |
| description | |
| format | Online Article Text |
| id | pubmed-9431580 |
| institution | National Center for Biotechnology Information |
| language | English |
| publishDate | 2022 |
| publisher | Lippincott Williams & Wilkins |
| record_format | MEDLINE/PubMed |
| spelling | pubmed-94315802022-08-31 PB2314: OLIPUDASE ALFA FOR ADULTS WITH ACID SPHINGOMYELINASE DEFICIENCY: IMPROVEMENTS IN CROSSOVER PLACEBO PATIENTS AND FURTHER IMPROVEMENTS IN ORIGINAL OLIPUDASE ALFA PATIENTS AFTER 2 YEARS IN ASCEND TRIAL Villarrubia, J. Wasserstein, M. Barbato, A. Gallagher, R. C. Giugliani, R. Guelbert, N. B. Hennermann, J. B. Hollak, C. Ikezoe, T. Lachmann, R. Lidove, O. Mabe, P. Mengel, E. Scarpa, M. Senates, E. Tchan, M. Thurberg, B. L. Yarramaneni, A. Rawlings, A. M. Kim, Y. Kumar, M. Hemasphere Publication Only Lippincott Williams & Wilkins 2022-06-23 /pmc/articles/PMC9431580/ http://dx.doi.org/10.1097/01.HS9.0000852080.43506.a5 Text en Copyright © 2022 The Author(s). Published by Wolters Kluwer Health, Inc. https://creativecommons.org/licenses/by-nc-nd/4.0/This is an open access Abstract Book distributed under the Attribution-NonCommercial-NoDerivs (CC BY-NC-ND) (https://creativecommons.org/licenses/by-nc-nd/4.0/) which allows third parties to download the articles and share them with others as long as they credit the author and the Abstract Book, but they cannot change the content in any way or use them commercially. |
| spellingShingle | Publication Only Villarrubia, J. Wasserstein, M. Barbato, A. Gallagher, R. C. Giugliani, R. Guelbert, N. B. Hennermann, J. B. Hollak, C. Ikezoe, T. Lachmann, R. Lidove, O. Mabe, P. Mengel, E. Scarpa, M. Senates, E. Tchan, M. Thurberg, B. L. Yarramaneni, A. Rawlings, A. M. Kim, Y. Kumar, M. PB2314: OLIPUDASE ALFA FOR ADULTS WITH ACID SPHINGOMYELINASE DEFICIENCY: IMPROVEMENTS IN CROSSOVER PLACEBO PATIENTS AND FURTHER IMPROVEMENTS IN ORIGINAL OLIPUDASE ALFA PATIENTS AFTER 2 YEARS IN ASCEND TRIAL |
| title | PB2314: OLIPUDASE ALFA FOR ADULTS WITH ACID SPHINGOMYELINASE DEFICIENCY: IMPROVEMENTS IN CROSSOVER PLACEBO PATIENTS AND FURTHER IMPROVEMENTS IN ORIGINAL OLIPUDASE ALFA PATIENTS AFTER 2 YEARS IN ASCEND TRIAL |
| title_full | PB2314: OLIPUDASE ALFA FOR ADULTS WITH ACID SPHINGOMYELINASE DEFICIENCY: IMPROVEMENTS IN CROSSOVER PLACEBO PATIENTS AND FURTHER IMPROVEMENTS IN ORIGINAL OLIPUDASE ALFA PATIENTS AFTER 2 YEARS IN ASCEND TRIAL |
| title_fullStr | PB2314: OLIPUDASE ALFA FOR ADULTS WITH ACID SPHINGOMYELINASE DEFICIENCY: IMPROVEMENTS IN CROSSOVER PLACEBO PATIENTS AND FURTHER IMPROVEMENTS IN ORIGINAL OLIPUDASE ALFA PATIENTS AFTER 2 YEARS IN ASCEND TRIAL |
| title_full_unstemmed | PB2314: OLIPUDASE ALFA FOR ADULTS WITH ACID SPHINGOMYELINASE DEFICIENCY: IMPROVEMENTS IN CROSSOVER PLACEBO PATIENTS AND FURTHER IMPROVEMENTS IN ORIGINAL OLIPUDASE ALFA PATIENTS AFTER 2 YEARS IN ASCEND TRIAL |
| title_short | PB2314: OLIPUDASE ALFA FOR ADULTS WITH ACID SPHINGOMYELINASE DEFICIENCY: IMPROVEMENTS IN CROSSOVER PLACEBO PATIENTS AND FURTHER IMPROVEMENTS IN ORIGINAL OLIPUDASE ALFA PATIENTS AFTER 2 YEARS IN ASCEND TRIAL |
| title_sort | pb2314: olipudase alfa for adults with acid sphingomyelinase deficiency: improvements in crossover placebo patients and further improvements in original olipudase alfa patients after 2 years in ascend trial |
| topic | Publication Only |
| url | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9431580/ http://dx.doi.org/10.1097/01.HS9.0000852080.43506.a5 |
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