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Decision-making about gene therapy in transfusion dependent thalassemia

BACKGROUND: Hematopoietic stem cell transplantation (HSCT) is a treatment option with curative intent for patients with transfusion dependent thalassemia (TDT) but its application is limited by the lack of suitable donors and acceptability due to the related morbidity/mortality. Transplantation of a...

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Detalles Bibliográficos
Autores principales:	Quarmyne, Maa-Ohui, Ross, Diana, Sinha, Cynthia, Bakshi, Nitya, Boudreaux, Jeanne, Krishnamurti, Lakshmanan
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2022
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9461218/ https://www.ncbi.nlm.nih.gov/pubmed/36085025 http://dx.doi.org/10.1186/s12887-022-03598-3

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