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A systematic review of economic evaluations of enzyme replacement therapy in Lysosomal storage diseases

OBJECTIVE: The objective of this paper is to assess the economic profile of enzyme replacement therapy (ERT) to symptomatic patients with Pompe, Fabry, Gaucher disease and Lysosomal acid lipase (LAL) deficiency. METHODS: A systematic search was performed to retrieve and critically assess economic ev...

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Detalles Bibliográficos
Autores principales:	Katsigianni, Eleni Ioanna, Petrou, Panagiotis
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2022
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9487102/ https://www.ncbi.nlm.nih.gov/pubmed/36123734 http://dx.doi.org/10.1186/s12962-022-00369-w

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