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Organoids and microphysiological systems: Promising models for accelerating AAV gene therapy studies
The FDA has predicted that at least 10-20 gene therapy products will be approved by 2025. The surge in the development of such therapies can be attributed to the advent of safe and effective gene delivery vectors such as adeno-associated virus (AAV). The enormous potential of AAV has been demonstrat...
Autores principales: | Ramamurthy, Ritu Mahesh, Atala, Anthony, Porada, Christopher D., Almeida-Porada, Graҫa |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2022
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9549755/ https://www.ncbi.nlm.nih.gov/pubmed/36225917 http://dx.doi.org/10.3389/fimmu.2022.1011143 |
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