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Real-world use of orphan medicinal products (OMPs) in rare disease (RD) patients: A population-based registry study

Background: Despite calls for the use of real-world data, the rare diseases (RD) treatment landscape suffers from a scarcity of data referred to orphan medicinal products (OMP) use at the population level. Objectives: We aim to describe the characteristics and patterns of utilization of OMP in a siz...

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Detalles Bibliográficos
Autores principales:	Mazzucato, Monica, Minichiello, Cinzia, Vianello, Andrea, Visonà dalla Pozza, Laura, Toto, Ema, Facchin, Paola
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Frontiers Media S.A. 2022
Materias:	Pharmacology
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9563616/ https://www.ncbi.nlm.nih.gov/pubmed/36249759 http://dx.doi.org/10.3389/fphar.2022.940010

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