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Base and Prime Editing in the Retina—From Preclinical Research toward Human Clinical Trials
Inherited retinal diseases (IRDs) are a clinically and genetically heterogeneous group of diseases that are one of the leading causes of vision loss in young and aged individuals. IRDs are mainly caused by a loss of the post-mitotic photoreceptor neurons of the retina, or by the degeneration of the...
Autores principales: | Yee, Tiffany, Wert, Katherine J. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2022
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9604474/ https://www.ncbi.nlm.nih.gov/pubmed/36293232 http://dx.doi.org/10.3390/ijms232012375 |
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