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Clinical and Electrophysiological Changes in Pediatric Spinal Muscular Atrophy after 2 Years of Nusinersen Treatment

In the new therapeutic era, disease-modifying treatment (nusinersen) has changed the natural evolution of spinal muscular atrophy (SMA), creating new phenotypes. The main purpose of the retrospective observational study was to explore changes in clinical evolution and electrophysiological data after...

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Detalles Bibliográficos
Autores principales:	Axente, Mihaela, Mirea, Andrada, Sporea, Corina, Pădure, Liliana, Drăgoi, Cristina Manuela, Nicolae, Alina Crenguța, Ion, Daniela Adriana
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2022
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9611420/ https://www.ncbi.nlm.nih.gov/pubmed/36297509 http://dx.doi.org/10.3390/pharmaceutics14102074

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