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OR18-5 A Prospective Clinical Trial of Vosoritide in Selected Genetic Causes of Short Stature

OBJECTIVES: Vosoritide is a C-type natriuretic peptide analog which binds its receptor on chondrocytes, leading to increased chondrocyte proliferation and differentiation via its inhibition of the ERK1/2-MAPK pathway. It was recently approved for increasing linear growth in children with achondropla...

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Detalles Bibliográficos
Autores principales:	Boucher, Kimberly, Dham, Niti, Kanakatti Shankar, Roopa, McCarthy, Tara, Merchant, Nadia, Zhang, Anqing, Dauber, Andrew
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Oxford University Press 2022
Materias:	Pediatric Endocrinology
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9625806/ http://dx.doi.org/10.1210/jendso/bvac150.1282

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