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Real-world experience of emicizumab prophylaxis in young children with hemophilia A: retrospective data from China

BACKGROUND: As a new non-factor therapy for hemophilia A (HA), real-world study of emicizumab is still scarce. This study aimed to investigate the real-world use of emicizumab in Chinese boys with HA. METHODS: Patients with moderate or severe HA were enrolled at Beijing Children's Hospital. The...

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Detalles Bibliográficos
Autores principales:	Liu, Guoqing, Huang, Kun, Li, Gang, Zhen, Yingzi, Li, Zhengping, Chen, Zhenping, Wu, Runhui
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Frontiers Media S.A. 2022
Materias:	Pediatrics
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9627604/ https://www.ncbi.nlm.nih.gov/pubmed/36340724 http://dx.doi.org/10.3389/fped.2022.992267

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