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Update on Viral Gene Therapy Clinical Trials for Retinal Diseases

In 2001, the first large animal was successfully treated with a gene therapy that restored its vision. Lancelot, the Briard dog that was treated, suffered from a human childhood blindness called Leber's congenital amaurosis type 2. Sixteen years later, the gene therapy was approved by the U.S....

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Detalles Bibliográficos
Autores principales: Cheng, Shun-Yun, Punzo, Claudio
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Mary Ann Liebert, Inc., publishers 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9639220/
https://www.ncbi.nlm.nih.gov/pubmed/36074935
http://dx.doi.org/10.1089/hum.2022.159