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Scoliosis in Spinal Muscular Atrophy Type 1 in the Nusinersen Era

BACKGROUND AND OBJECTIVES: The introduction of spinal muscular dystrophy (SMA)-modifying therapies, such as antisense oligonucleotide therapy, has changed the natural history of SMA. Most reports on treatment outcomes have focused on motor scores and respiratory function. The objective of this study...

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Detalles Bibliográficos
Autores principales:	Al Amrani, Fatima, Amin, Reshma, Chiang, Jackie, Xiao, Lena, Boyd, Jennifer, Law, Eugenia, Nigro, Elisa, Weinstock, Lauren, Stosic, Ana, Gonorazky, Hernan D.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Lippincott Williams & Wilkins 2022
Materias:	Research Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9647826/ https://www.ncbi.nlm.nih.gov/pubmed/36382115 http://dx.doi.org/10.1212/CPJ.0000000000001179

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