Cargando…

Dual CFTR modulator therapy efficacy in the real world: lessons for the future

Stringent analyses caution against drawing conclusions about the real-world efficacy of CFTR modulator therapy too early https://bit.ly/3dJt6no

Detalles Bibliográficos
Autores principales:	Dittrich, Anna-Maria, Chuang, Sandra Y.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	European Respiratory Society 2022
Materias:	Editorials
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9661234/ https://www.ncbi.nlm.nih.gov/pubmed/36382239 http://dx.doi.org/10.1183/23120541.00464-2022

Ejemplares similares

New therapies for people with CF in the CFTR modulator world
por: Wainwright, Claire E
Publicado: (2020)

Editorial: Real-world experience with CFTR modulator therapy
por: Tümmler, Burkhard, et al.
Publicado: (2023)

The PROSPECT Is Bright for CFTR Modulators
por: Montemayor, Kristina, et al.
Publicado: (2021)

CFTR Modulators in People with Cystic Fibrosis: Real-World Evidence in France
por: Regard, Lucile, et al.
Publicado: (2022)

Real-World Safety of CFTR Modulators in the Treatment of Cystic Fibrosis: A Systematic Review
por: Dagenais, Renée V. E., et al.
Publicado: (2020)

Real-world disparities and ethical considerations with access to CFTR modulator drugs: Mind the gap!
por: Zampoli, M., et al.
Publicado: (2023)

How Should the Effects of CFTR Modulator Therapy on Cystic Fibrosis Lung Disease Be Monitored?
por: Ben-Meir, Elad, et al.
Publicado: (2022)

Putting CHIP(s) on the Table: Introducing Nitrosothiols into the Arena of CFTR Modulation
por: Addy, Charlotte, et al.
Publicado: (2019)

Impact of Airway Inflammation on the Efficacy of CFTR Modulators
por: Ribeiro, Carla M. P., et al.
Publicado: (2021)

CFTR Modulators to the Rescue of Individuals with Cystic Fibrosis and Advanced Lung Disease
por: Myerburg, Mike, et al.
Publicado: (2021)

Real-life impact of highly effective CFTR modulator therapy in children with cystic fibrosis
por: Olivier, Margarete, et al.
Publicado: (2023)

Triplet CFTR modulators: future prospects for treatment of cystic fibrosis
por: Chaudary, Nauman
Publicado: (2018)

Long-term effectiveness of dual CFTR modulator treatment of cystic fibrosis
por: Muilwijk, Danya, et al.
Publicado: (2022)

MitraClip Real-World Data: What Is Missing and Looking Into the Future
por: Mesana, Thierry G.
Publicado: (2020)

Lessons From India’s Second Wave: Real World Effectiveness of Health Care Worker Vaccination
por: Sampathkumar, Priya
Publicado: (2021)

CFTR modulators: transformative therapies for cystic fibrosis
por: Dwight, Mary, et al.
Publicado: (2021)

Airway Epithelial Inflammation In Vitro Augments the Rescue of Mutant CFTR by Current CFTR Modulator Therapies
por: Gentzsch, Martina, et al.
Publicado: (2021)

Lesson from Real-World Experience: Optimal Treatment with Anti-Tumor Necrosis Factor for Ulcerative Colitis
por: Chun, Jaeyoung
Publicado: (2021)

Opening CFTR in the Intestine: Flushing on Demand
por: Lencer, Wayne I.
Publicado: (2016)

CFTR and the Regulation of Crypt Cell Proliferation
por: Rubin, Deborah C.
Publicado: (2018)

Pharmacological Responses of the G542X-CFTR to CFTR Modulators
por: Fang, Xinxiu, et al.
Publicado: (2022)

Integrity and Stability of PTC Bearing CFTR mRNA and Relevance to Future Modulator Therapies in Cystic Fibrosis
por: Clarke, Luka A., et al.
Publicado: (2021)

Gene Therapy: A Possible Alternative to CFTR Modulators?
por: Mercier, J., et al.
Publicado: (2021)

Prediction of Real-World Long-Term Outcomes of People with CF Homozygous for the F508del Mutation Treated with CFTR Modulators
por: Muilwijk, Danya, et al.
Publicado: (2021)

An Update on CFTR Drug Discovery: Opportunities and Challenges
por: D’Ursi, Pasqualina, et al.
Publicado: (2022)

Osteosarcoma: Lessons Learned and Future Avenues
por: Puri, Ajay, et al.
Publicado: (2013)

Lessons from COVID and looking to the future
por: Kay, Elizabeth
Publicado: (2020)

World Sickle Cell Day: Lessons for India
por: Serjeant, Graham
Publicado: (2017)

Of muscle modulation and the CFTR gate
por: Adler, Elizabeth M.
Publicado: (2015)

Memory Self-Efficacy Beliefs Modulate Brain Activity when Encoding Real-World Future Intentions
por: Kalpouzos, Grégoria, et al.
Publicado: (2013)

Recent Developments in Cancer Systems Biology: Lessons Learned and Future Directions
por: Arga, Kazim Y., et al.
Publicado: (2021)

Ex vivo model predicted in vivo efficacy of CFTR modulator therapy in a child with rare genotype
por: Terlizzi, Vito, et al.
Publicado: (2021)

Learning lessons from the COVID-19 pandemic for real-world evidence research in oncology—shared perspectives from international consortia
por: Castelo-Branco, L., et al.
Publicado: (2023)

Peritoneal Dialysis in the United States: Lessons for the Future
por: Hansson, Joni H., et al.
Publicado: (2020)

COVID-19: Lost opportunities and lessons for the future
por: Saqr, Mohammed, et al.
Publicado: (2020)

World Immunization Week 2018: What lessons for India?
por: John, T. Jacob
Publicado: (2018)

The Future of Highly Effective Modulator Therapy in Cystic Fibrosis
por: Daines, Cori L., et al.
Publicado: (2021)

Lessons Learned from Randomized Trials and Recent Experience with Health Information Technology: Promising Interventions Meet Real-World Patient Care
por: Fairman, Kathleen A., et al.
Publicado: (2010)

Drugs: Real World Outcomes
por: Peters, Dene C., et al.
Publicado: (2014)

Real‐world effectiveness of antipsychotics
por: Tiihonen, J.
Publicado: (2016)

Cannot write session to /tmp/vufind_sessions/sess_9gbrtoiasd0q394ie8vg7pqdpm