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Long-term effectiveness of dual CFTR modulator treatment of cystic fibrosis

BACKGROUND: Although short-term efficacy of lumacaftor/ivacaftor and tezacaftor/ivacaftor is clearly established in clinical trials, data on long-term effectiveness is limited. This registry-based cohort study assessed real-world longitudinal outcomes of F508del-homozygous people with cystic fibrosi...

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Detalles Bibliográficos
Autores principales:	Muilwijk, Danya, Zomer-van Ommen, Domenique D., Gulmans, Vincent A.M., Eijkemans, Marinus J.C., van der Ent, Cornelis K.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	European Respiratory Society 2022
Materias:	Original Research Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9661249/ https://www.ncbi.nlm.nih.gov/pubmed/36382237 http://dx.doi.org/10.1183/23120541.00204-2022

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