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Current advances in gene therapy of mitochondrial diseases

Mitochondrial diseases (MD) are a heterogeneous group of multisystem disorders involving metabolic errors. MD are characterized by extremely heterogeneous symptoms, ranging from organ-specific to multisystem dysfunction with different clinical courses. Most primary MD are autosomal recessive but mat...

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Detalles Bibliográficos
Autores principales:	Soldatov, Vladislav O., Kubekina, Marina V., Skorkina, Marina Yu., Belykh, Andrei E., Egorova, Tatiana V., Korokin, Mikhail V., Pokrovskiy, Mikhail V., Deykin, Alexey V., Angelova, Plamena R.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2022
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9724384/ https://www.ncbi.nlm.nih.gov/pubmed/36471396 http://dx.doi.org/10.1186/s12967-022-03685-0

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