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Are We Getting It Right? A Scoping Review of Outcomes Reported in Cell Therapy Clinical Studies for Cerebral Palsy

Cell therapies are an emergent treatment for cerebral palsy (CP) with promising evidence demonstrating efficacy for improving gross motor function. However, families value improvements in a range of domains following intervention and the non-motor symptoms, comorbidities and complications of CP can...

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Autores principales: Finch-Edmondson, Megan, Paton, Madison C. B., Honan, Ingrid, Karlsson, Petra, Stephenson, Candice, Chiu, Darryl, Reedman, Sarah, Griffin, Alexandra R., Morgan, Catherine, Novak, Iona
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9786692/
https://www.ncbi.nlm.nih.gov/pubmed/36555936
http://dx.doi.org/10.3390/jcm11247319
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author Finch-Edmondson, Megan
Paton, Madison C. B.
Honan, Ingrid
Karlsson, Petra
Stephenson, Candice
Chiu, Darryl
Reedman, Sarah
Griffin, Alexandra R.
Morgan, Catherine
Novak, Iona
author_facet Finch-Edmondson, Megan
Paton, Madison C. B.
Honan, Ingrid
Karlsson, Petra
Stephenson, Candice
Chiu, Darryl
Reedman, Sarah
Griffin, Alexandra R.
Morgan, Catherine
Novak, Iona
author_sort Finch-Edmondson, Megan
collection PubMed
description Cell therapies are an emergent treatment for cerebral palsy (CP) with promising evidence demonstrating efficacy for improving gross motor function. However, families value improvements in a range of domains following intervention and the non-motor symptoms, comorbidities and complications of CP can potentially be targeted by cell therapies. We conducted a scoping review to describe all outcomes that have been reported in cell therapy studies for CP to date, and to examine what instruments were used to capture these. Through a systematic search we identified 54 studies comprising 2066 participants that were treated with a range of cell therapy interventions. We categorized the reported 53 unique outcome instruments and additional descriptive measures into 10 categories and 12 sub-categories. Movement and Posture was the most frequently reported outcome category, followed by Safety, however Quality of Life, and various prevalent comorbidities and complications of CP were infrequently reported. Notably, many outcome instruments used do not have evaluative properties and thus are not suitable for measuring change following intervention. We provide a number of recommendations to ensure that future trials generate high-quality outcome data that is aligned with the priorities of the CP community.
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spelling pubmed-97866922022-12-24 Are We Getting It Right? A Scoping Review of Outcomes Reported in Cell Therapy Clinical Studies for Cerebral Palsy Finch-Edmondson, Megan Paton, Madison C. B. Honan, Ingrid Karlsson, Petra Stephenson, Candice Chiu, Darryl Reedman, Sarah Griffin, Alexandra R. Morgan, Catherine Novak, Iona J Clin Med Review Cell therapies are an emergent treatment for cerebral palsy (CP) with promising evidence demonstrating efficacy for improving gross motor function. However, families value improvements in a range of domains following intervention and the non-motor symptoms, comorbidities and complications of CP can potentially be targeted by cell therapies. We conducted a scoping review to describe all outcomes that have been reported in cell therapy studies for CP to date, and to examine what instruments were used to capture these. Through a systematic search we identified 54 studies comprising 2066 participants that were treated with a range of cell therapy interventions. We categorized the reported 53 unique outcome instruments and additional descriptive measures into 10 categories and 12 sub-categories. Movement and Posture was the most frequently reported outcome category, followed by Safety, however Quality of Life, and various prevalent comorbidities and complications of CP were infrequently reported. Notably, many outcome instruments used do not have evaluative properties and thus are not suitable for measuring change following intervention. We provide a number of recommendations to ensure that future trials generate high-quality outcome data that is aligned with the priorities of the CP community. MDPI 2022-12-09 /pmc/articles/PMC9786692/ /pubmed/36555936 http://dx.doi.org/10.3390/jcm11247319 Text en © 2022 by the authors. https://creativecommons.org/licenses/by/4.0/Licensee MDPI, Basel, Switzerland. This article is an open access article distributed under the terms and conditions of the Creative Commons Attribution (CC BY) license (https://creativecommons.org/licenses/by/4.0/).
spellingShingle Review
Finch-Edmondson, Megan
Paton, Madison C. B.
Honan, Ingrid
Karlsson, Petra
Stephenson, Candice
Chiu, Darryl
Reedman, Sarah
Griffin, Alexandra R.
Morgan, Catherine
Novak, Iona
Are We Getting It Right? A Scoping Review of Outcomes Reported in Cell Therapy Clinical Studies for Cerebral Palsy
title Are We Getting It Right? A Scoping Review of Outcomes Reported in Cell Therapy Clinical Studies for Cerebral Palsy
title_full Are We Getting It Right? A Scoping Review of Outcomes Reported in Cell Therapy Clinical Studies for Cerebral Palsy
title_fullStr Are We Getting It Right? A Scoping Review of Outcomes Reported in Cell Therapy Clinical Studies for Cerebral Palsy
title_full_unstemmed Are We Getting It Right? A Scoping Review of Outcomes Reported in Cell Therapy Clinical Studies for Cerebral Palsy
title_short Are We Getting It Right? A Scoping Review of Outcomes Reported in Cell Therapy Clinical Studies for Cerebral Palsy
title_sort are we getting it right? a scoping review of outcomes reported in cell therapy clinical studies for cerebral palsy
topic Review
url https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9786692/
https://www.ncbi.nlm.nih.gov/pubmed/36555936
http://dx.doi.org/10.3390/jcm11247319
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