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Hematopoietic Stem Cell Transplantation in CSF1R-Related Leukoencephalopathy: Retrospective Study on Predictors of Outcomes

Mutations in the CSF1R gene are the most common cause of adult-onset leukoencephalopathy with axonal spheroids and pigmented glia (ALSP), a neurodegenerative disease with rapid progression and ominous prognosis. Hematopoietic stem cell transplantation (HSCT) has been increasingly offered to patients...

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Detalles Bibliográficos
Autores principales:	Dulski, Jarosław, Heckman, Michael G., White, Launia J., Żur-Wyrozumska, Kamila, Lund, Troy C., Wszolek, Zbigniew K.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2022
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9788080/ https://www.ncbi.nlm.nih.gov/pubmed/36559271 http://dx.doi.org/10.3390/pharmaceutics14122778

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