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Comprehensive profile and natural history of pediatric patients with spinal muscular atrophy: A large retrospective study from China

BACKGROUND: There is a large population of people with spinal muscular atrophy (SMA) in China, and new disease-modifying therapies have become available recently. However, comprehensive data on the management and profile of treatment-naive SMA patients in China are still lacking. METHODS: As a retro...

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Detalles Bibliográficos
Autores principales:	Hu, Chaoping, Li, Xihua, Shi, Yiyun, Zhu, Xiaomei, Zhao, Lei, Li, Wenhui, Zhou, Shuizhen, Wang, Yi
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Frontiers Media S.A. 2022
Materias:	Neurology
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9810274/ https://www.ncbi.nlm.nih.gov/pubmed/36605788 http://dx.doi.org/10.3389/fneur.2022.1038012

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