Randomized double-blind placebo-controlled crossover trial with pyridostigmine in spinal muscular atrophy types 2–4

Hereditary proximal spinal muscular atrophy causes weakness and increased fatigability of repetitive motor functions. The neuromuscular junction is anatomically and functionally abnormal in patients with spinal muscular atrophy. Pharmacological improvement of neuromuscular transmission may therefore...

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Detalles Bibliográficos
Autores principales: Stam, Marloes, Wijngaarde, Camiel A, Bartels, Bart, Asselman, Fay-Lynn, Otto, Louise A M, Habets, Laura E, van Eijk, Ruben P A, Middelkoop, Bas M, Goedee, H Stephan, de Groot, Janke F, Roes, Kit C B, Schoenmakers, Marja A G C, Nieuwenhuis, Edward E S, Cuppen, Inge, van den Berg, Leonard H, Wadman, Renske I, van der Pol, W Ludo
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Oxford University Press 2022
Materias:
Original Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9825780/
https://www.ncbi.nlm.nih.gov/pubmed/36632180
http://dx.doi.org/10.1093/braincomms/fcac324

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