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Validation of motor and functional scales for the evaluation of adult patients with 5q spinal muscular atrophy
BACKGROUND AND PURPOSE: Mos scales currently used to evaluate spinal muscular atrophy (SMA) patients have only been validated in children. The aim of this study was to assess the construct validity and responsiveness of several outcome measures in adult SMA patients. METHODS: Patients older than 15 ...
Autores principales: | Vázquez‐Costa, Juan F., Povedano, Mónica, Nascimiento‐Osorio, Andrés E., Moreno Escribano, Antonio, Kapetanovic Garcia, Solange, Dominguez, Raul, Exposito, Jessica M., González, Laura, Marco, Carla, Medina Castillo, Julita, Muelas, Nuria, Natera de Benito, Daniel, Ñungo Garzón, Nancy Carolina, Pitarch Castellano, Inmaculada, Sevilla, Teresa, Hervás, David |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
John Wiley and Sons Inc.
2022
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9826246/ https://www.ncbi.nlm.nih.gov/pubmed/36047967 http://dx.doi.org/10.1111/ene.15542 |
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