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Cerebrospinal fluid characteristics of patients treated with intrathecal nusinersen for spinal muscular atrophy

INTRODUCTION/AIMS: There is limited information on the potential effects of repeated intrathecal antisense oligonucleotide drug delivery on cerebrospinal fluid (CSF) biochemical and blood cell profiles. This study aimed to examine longitudinal changes in the biochemical components (glucose, protein)...

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Detalles Bibliográficos
Autores principales:	Orbach, Rotem, Sagi, Liora, Sadot, Efraim, Tokatly Latzer, Itay, Shtamler, Anna, Zisberg, Tehila, Fattal‐Valevski, Aviva
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	John Wiley & Sons, Inc. 2022
Materias:	Clinical Research Short Reports
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9828332/ https://www.ncbi.nlm.nih.gov/pubmed/36214191 http://dx.doi.org/10.1002/mus.27731

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