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One-year results of a clinical trial of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency
| Autores principales: | , , , , , , , , , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
Elsevier
2022
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| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9829548/ https://www.ncbi.nlm.nih.gov/pubmed/36205749 http://dx.doi.org/10.1016/j.gim.2022.08.011 |
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| author | Diaz, George A. Jones, Simon A. Scarpa, Maurizio Mengel, Karl Eugen Giugliani, Roberto Guffon, Nathalie Batsu, Isabela Fraser, Patricia A. Li, Jing Zhang, Qi Ortemann-Renon, Catherine |
| author_facet | Diaz, George A. Jones, Simon A. Scarpa, Maurizio Mengel, Karl Eugen Giugliani, Roberto Guffon, Nathalie Batsu, Isabela Fraser, Patricia A. Li, Jing Zhang, Qi Ortemann-Renon, Catherine |
| author_sort | Diaz, George A. |
| collection | PubMed |
| description | |
| format | Online Article Text |
| id | pubmed-9829548 |
| institution | National Center for Biotechnology Information |
| language | English |
| publishDate | 2022 |
| publisher | Elsevier |
| record_format | MEDLINE/PubMed |
| spelling | pubmed-98295482023-01-10 One-year results of a clinical trial of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency Diaz, George A. Jones, Simon A. Scarpa, Maurizio Mengel, Karl Eugen Giugliani, Roberto Guffon, Nathalie Batsu, Isabela Fraser, Patricia A. Li, Jing Zhang, Qi Ortemann-Renon, Catherine Genet Med Erratum Elsevier 2022-10 /pmc/articles/PMC9829548/ /pubmed/36205749 http://dx.doi.org/10.1016/j.gim.2022.08.011 Text en © 2022 Published by Elsevier Inc. on behalf of American College of Medical Genetics and Genomics. https://creativecommons.org/licenses/by-nc-nd/4.0/This is an open access article under the CC BY-NC-ND license (http://creativecommons.org/licenses/by-nc-nd/4.0/). |
| spellingShingle | Erratum Diaz, George A. Jones, Simon A. Scarpa, Maurizio Mengel, Karl Eugen Giugliani, Roberto Guffon, Nathalie Batsu, Isabela Fraser, Patricia A. Li, Jing Zhang, Qi Ortemann-Renon, Catherine One-year results of a clinical trial of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency |
| title | One-year results of a clinical trial of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency |
| title_full | One-year results of a clinical trial of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency |
| title_fullStr | One-year results of a clinical trial of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency |
| title_full_unstemmed | One-year results of a clinical trial of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency |
| title_short | One-year results of a clinical trial of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency |
| title_sort | one-year results of a clinical trial of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency |
| topic | Erratum |
| url | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9829548/ https://www.ncbi.nlm.nih.gov/pubmed/36205749 http://dx.doi.org/10.1016/j.gim.2022.08.011 |
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