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Development of Lanzyme as the Potential Enzyme Replacement Therapy Drug for Fabry Disease

Fabry disease (FD) is a progressive multisystemic disease characterized by lysosomal enzyme deficiency. Enzyme replacement therapy (ERT) is one of the most significant advancements and breakthroughs in treating FD. However, limited resources and the high cost of ERT might prevent patients from recei...

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Detalles Bibliográficos
Autores principales:	Deng, Mulan, Zhou, Hongyu, Liang, Zhicheng, Li, Zhaoyang, Wang, Yanping, Guo, Wanyi, Zhao, April Yuanyi, Li, Fanghong, Mu, Yunping, Zhao, Allan Zijian
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2022
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9855849/ https://www.ncbi.nlm.nih.gov/pubmed/36671438 http://dx.doi.org/10.3390/biom13010053

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