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Gene Therapy in ALS and SMA: Advances, Challenges and Perspectives

Gene therapy is defined as the administration of genetic material to modify, manipulate gene expression or alter the properties of living cells for therapeutic purposes. Recent advances and improvements in this field have led to many breakthroughs in the treatment of various diseases. As a result, t...

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Detalles Bibliográficos
Autores principales:	Lejman, Jan, Panuciak, Kinga, Nowicka, Emilia, Mastalerczyk, Angelika, Wojciechowska, Katarzyna, Lejman, Monika
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2023
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9860634/ https://www.ncbi.nlm.nih.gov/pubmed/36674643 http://dx.doi.org/10.3390/ijms24021130

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