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Identification of Novel CSF-Derived miRNAs in Treated Paediatric Onset Spinal Muscular Atrophy: An Exploratory Study

The availability of disease modifying therapies for spinal muscular atrophy (SMA) have created an urgent need to identify clinically meaningful biomarkers that provide insight into disease progression and therapeutic response. microRNAs (miRNA) have been shown to be involved in the pathogenesis of S...

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Detalles Bibliográficos
Autores principales:	D’Silva, Arlene M., Kariyawasam, Didu, Venkat, Pooja, Mayoh, Chelsea, Farrar, Michelle A.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2023
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9865256/ https://www.ncbi.nlm.nih.gov/pubmed/36678797 http://dx.doi.org/10.3390/pharmaceutics15010170

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