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Clinical genome editing to treat sickle cell disease—A brief update

Sickle cell disease (SCD) is one of the most common hemoglobinopathies. Due to its high prevalence, with about 20 million affected individuals worldwide, the development of novel effective treatments is highly warranted. While transplantation of allogeneic hematopoietic stem cells (HSC) is the stand...

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Detalles Bibliográficos
Autores principales:	Zarghamian, Parinaz, Klermund, Julia, Cathomen, Toni
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Frontiers Media S.A. 2023
Materias:	Medicine
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9868311/ https://www.ncbi.nlm.nih.gov/pubmed/36698803 http://dx.doi.org/10.3389/fmed.2022.1065377

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