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Case report: Venetoclax therapy in a boy with acute myeloid leukemia in Shwachman Diamond syndrome
Shwachman-Diamond syndrome (SDS) is a rare bone marrow failure syndrome characterized by exocrine pancreatic insufficiency, bone abnormalities, progressive cytopenia, and predispositions to myelodysplastic syndrome (MDS) and acute myeloid leukemia (AML). AML, in these patients, is associated with a...
Autores principales: | Naviglio, Samuele, Grasso, Antonio Giacomo, Iacono, Chiara, Zanella, Giada, Kiren, Valentina, Giurici, Nagua, Verzegnassi, Federico, Maximova, Natalia, Rabusin, Marco |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9869240/ https://www.ncbi.nlm.nih.gov/pubmed/36699295 http://dx.doi.org/10.3389/fped.2022.1059569 |
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