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Hematopoietic Stem Cell Transplantation is a cost-effective alternative to enzyme replacement therapy in Gaucher Disease

Allogeneic hematopoietic stem cell transplantation (HSCT) is a feasible treatment option for Gaucher disease (GD). Among 60 patients diagnosed with GD over 15 years (2004-2019), three children who underwent HSCT (January-November 2017) were analyzed. Two boys (cases 1 and 2) and one girl (case 3) re...

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Detalles Bibliográficos
Autores principales:	Aboobacker, Fouzia N, Kulkarni, Uday P, Korula, Anu, Devasia, Anup J, Selvarajan, Sushil, Lionel, Sharon, Sindhuvi, Eunice, Srivastava, Alok, George, Biju, Abraham, Aby
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Asia-Pacific Blood and Marrow Transplantation Group 2022
Materias:	Original Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9873422/ https://www.ncbi.nlm.nih.gov/pubmed/36712555 http://dx.doi.org/10.31547/bct-2021-020

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