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Functional and Clinical Outcomes Associated with Steroid Treatment among Non-ambulatory Patients with Duchenne Muscular Dystrophy(1)
BACKGROUND: Evidence on the long-term efficacy of steroids in Duchenne muscular dystrophy (DMD) after loss of ambulation is limited. OBJECTIVE: Characterize and compare disease progression by steroid treatment (prednisone, deflazacort, or no steroids) among non-ambulatory boys with DMD. METHODS: Dis...
Autores principales: | McDonald, Craig M., Mayer, Oscar H., Hor, Kan N., Miller, Debra, Goemans, Nathalie, Henricson, Erik K., Marden, Jessica R., Freimark, Jonathan, Lane, Henry, Zhang, Adina, Frean, Molly, Trifillis, Panayiota, Koladicz, Karyn, Signorovitch, James |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
IOS Press
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9881035/ https://www.ncbi.nlm.nih.gov/pubmed/36565131 http://dx.doi.org/10.3233/JND-221575 |
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