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Lentiviral Gene Transfer Corrects Immune Abnormalities in XIAP Deficiency

BACKGROUND: X-linked inhibitor of apoptosis protein (XIAP) deficiency is a severe immunodeficiency with clinical features including hemophagocytic lymphohistiocytosis (HLH) and inflammatory bowel disease (IBD) due to defective NOD2 responses. Management includes immunomodulatory therapies and hemato...

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Detalles Bibliográficos
Autores principales:	Topal, Joseph, Panchal, Neelam, Barroeta, Amairelys, Roppelt, Anna, Mudde, Annelotte, Gaspar, H. Bobby, Thrasher, Adrian J., Houghton, Benjamin C., Booth, Claire
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer US 2022
Materias:	Original Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9892131/ https://www.ncbi.nlm.nih.gov/pubmed/36329240 http://dx.doi.org/10.1007/s10875-022-01389-0

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