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Changes in Retinal Sensitivity Associated With Cotoretigene Toliparvovec in X-Linked Retinitis Pigmentosa With RPGR Gene Variations

IMPORTANCE: X-linked retinitis pigmentosa (XLRP) is a severe cause of early-onset RP in male individuals, characterized by degeneration of photoreceptors, an extinguished electroretinogram, and vision loss. OBJECTIVE: To assess the duration of improvements in retinal sensitivity associated with a si...

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Detalles Bibliográficos
Autores principales:	von Krusenstiern, Lenore, Liu, Jiajun, Liao, Eileen, Gow, James A., Chen, Guo, Ong, Tuyen, Lotery, Andrew J., Jalil, Assad, Lam, Byron L., MacLaren, Robert E.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	American Medical Association 2023
Materias:	Original Investigation
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9912164/ https://www.ncbi.nlm.nih.gov/pubmed/36757689 http://dx.doi.org/10.1001/jamaophthalmol.2022.6254

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