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Future Perspectives of Prime Editing for the Treatment of Inherited Retinal Diseases

Inherited retinal diseases (IRD) are a clinically and genetically heterogenous group of diseases and a leading cause of blindness in the working-age population. Even though gene augmentation therapies have shown promising results, they are only feasible to treat a small number of autosomal recessive...

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Detalles Bibliográficos
Autores principales:	Hansen, Silja, McClements, Michelle E., Corydon, Thomas J., MacLaren, Robert E.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2023
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9913839/ https://www.ncbi.nlm.nih.gov/pubmed/36766782 http://dx.doi.org/10.3390/cells12030440

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