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Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle

Dystrophin is essential for muscle health: its sarcolemmal absence causes the fatal, X-linked condition, Duchenne muscular dystrophy (DMD). However, its normal, spatial organization remains poorly understood, which hinders the interpretation of efficacy of its therapeutic restoration. Using female r...

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Detalles Bibliográficos
Autores principales:	Morin, Adrien, Stantzou, Amalia, Petrova, Olga N., Hildyard, John, Tensorer, Thomas, Matouk, Meriem, Petkova, Mina V., Richard, Isabelle, Manoliu, Tudor, Goyenvalle, Aurélie, Falcone, Sestina, Schuelke, Markus, Laplace-Builhé, Corinne, Piercy, Richard J., Garcia, Luis, Amthor, Helge
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	National Academy of Sciences 2023
Materias:	Biological Sciences
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9926233/ https://www.ncbi.nlm.nih.gov/pubmed/36595689 http://dx.doi.org/10.1073/pnas.2206324120

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