Areas of improvement in the medical care of SMA: evidence from a nationwide patient registry in Germany

BACKGROUND: Management and treatment of spinal muscular atrophy (SMA) has changed in recent years due to the introduction of novel transformative and potentially curative therapies resulting in the emergence of new disease phenotypes. Yet, little is known about the uptake and impact of these therapi...

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Detalles Bibliográficos
Autores principales: Leibrock, Berenike, Landfeldt, Erik, Hussong, Justine, Huelle, Tabea, Mattheus, Hannah, Thiele, Simone, Walter, Maggie C., Zemlin, Michael, Moehler, Eva, Dillman, Ullrich, Abner, Sophia, Flotats-Bastardas, Marina
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BioMed Central 2023
Materias:
Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9945617/
https://www.ncbi.nlm.nih.gov/pubmed/36810103
http://dx.doi.org/10.1186/s13023-023-02639-z

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9945617/
https://www.ncbi.nlm.nih.gov/pubmed/36810103
http://dx.doi.org/10.1186/s13023-023-02639-z

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